OtherDrug Discovery and Translational Medicine
Tralesinidase alfa enzyme replacement therapy prevents disease manifestations in a canine model of mucopolysaccharidosis type IIIB
N. Matthew Ellinwood, Bethann N Valentine, Andrew S Hess, Jackie K Jens, Elizabeth M Snella, Maryam Jamil, Shannon J Hostetter, Nicholas D Jeffery, Jodi D Smith, Suzanne T Millman, Rebecca L Parsons, Mark T Butt, Sundeep Chandra, Martin T Egeland, Ana B Assis, Hemanth R Nelvagal, Jonathan D Cooper, Igor Nestrasil, Bryon A Mueller, Rene Labounek, Amy Paulson, Heather Prill, Xiao Ying Liu, Huiyu Zhou, Roger Lawrence, Brett E Crawford, Anita Grover, Ganesh Cherala, Andrew C Melton, Anu Cherukuri, Brian R Vuillemenot, Jill CM Wait, Charles A. O'Neill, Jason Pinkstaff, Joseph Kovalchin, Eric Zanelli and Emma McCullagh
Journal of Pharmacology and Experimental Therapeutics June 18, 2022, JPET-AR-2022-001119; DOI: https://doi.org/10.1124/jpet.122.001119
N. Matthew Ellinwood
1Departments of Animal Science and Veterinary Clinical Science, Iowa State University, United States
Bethann N Valentine
2Departnment of Animal Science, Iowa State University, United States
Andrew S Hess
2Departnment of Animal Science, Iowa State University, United States
Jackie K Jens
3Department of Animal Science, Iowa State University, United States
Elizabeth M Snella
3Department of Animal Science, Iowa State University, United States
Maryam Jamil
3Department of Animal Science, Iowa State University, United States
Shannon J Hostetter
4Department of Veterinary Pathology, Iowa State University, United States
Nicholas D Jeffery
5Department of Veterinary Clinical Science, Iowa State University, United States
Jodi D Smith
4Department of Veterinary Pathology, Iowa State University, United States
Suzanne T Millman
6Department of Veterinary Diagnostics and Production Animal Medicine and Department of Biomedical Science, Iowa State University, United States
Rebecca L Parsons
7Department of Veterinary Diagnostics and Production Animal Medicine, Iowa State University, United States
Mark T Butt
8StageBio, United States
Sundeep Chandra
9BioMarin Pharmaceutical Inc., United States
Martin T Egeland
10The Lundquist Institute (formerly Los Angeles Biomedical Research Institute, Harbor-UCLA Medical Center, United States
Ana B Assis
10The Lundquist Institute (formerly Los Angeles Biomedical Research Institute, Harbor-UCLA Medical Center, United States
Hemanth R Nelvagal
10The Lundquist Institute (formerly Los Angeles Biomedical Research Institute, Harbor-UCLA Medical Center, United States
Jonathan D Cooper
10The Lundquist Institute (formerly Los Angeles Biomedical Research Institute, Harbor-UCLA Medical Center, United States
Igor Nestrasil
11University of Minnesota, Department of Pediatrics, United States
Bryon A Mueller
11University of Minnesota, Department of Pediatrics, United States
Rene Labounek
11University of Minnesota, Department of Pediatrics, United States
Amy Paulson
11University of Minnesota, Department of Pediatrics, United States
Heather Prill
9BioMarin Pharmaceutical Inc., United States
Xiao Ying Liu
9BioMarin Pharmaceutical Inc., United States
Huiyu Zhou
9BioMarin Pharmaceutical Inc., United States
Roger Lawrence
9BioMarin Pharmaceutical Inc., United States
Brett E Crawford
9BioMarin Pharmaceutical Inc., United States
Anita Grover
9BioMarin Pharmaceutical Inc., United States
Ganesh Cherala
9BioMarin Pharmaceutical Inc., United States
Andrew C Melton
9BioMarin Pharmaceutical Inc., United States
Anu Cherukuri
9BioMarin Pharmaceutical Inc., United States
Brian R Vuillemenot
9BioMarin Pharmaceutical Inc., United States
Jill CM Wait
9BioMarin Pharmaceutical Inc., United States
Charles A. O'Neill
12Pharmacological Sciences, BioMarin Pharmaceutical Inc., United States
Jason Pinkstaff
9BioMarin Pharmaceutical Inc., United States
Joseph Kovalchin
13Allievex Corporation, United States
Eric Zanelli
13Allievex Corporation, United States
Emma McCullagh
9BioMarin Pharmaceutical Inc., United States
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In this issue
OtherDrug Discovery and Translational Medicine
Efficacy of tralesinidase alfa in a canine model of MPS IIIB
N. Matthew Ellinwood, Bethann N Valentine, Andrew S Hess, Jackie K Jens, Elizabeth M Snella, Maryam Jamil, Shannon J Hostetter, Nicholas D Jeffery, Jodi D Smith, Suzanne T Millman, Rebecca L Parsons, Mark T Butt, Sundeep Chandra, Martin T Egeland, Ana B Assis, Hemanth R Nelvagal, Jonathan D Cooper, Igor Nestrasil, Bryon A Mueller, Rene Labounek, Amy Paulson, Heather Prill, Xiao Ying Liu, Huiyu Zhou, Roger Lawrence, Brett E Crawford, Anita Grover, Ganesh Cherala, Andrew C Melton, Anu Cherukuri, Brian R Vuillemenot, Jill CM Wait, Charles A. O'Neill, Jason Pinkstaff, Joseph Kovalchin, Eric Zanelli and Emma McCullagh
Journal of Pharmacology and Experimental Therapeutics June 18, 2022, JPET-AR-2022-001119; DOI: https://doi.org/10.1124/jpet.122.001119
OtherDrug Discovery and Translational Medicine
Efficacy of tralesinidase alfa in a canine model of MPS IIIB
N. Matthew Ellinwood, Bethann N Valentine, Andrew S Hess, Jackie K Jens, Elizabeth M Snella, Maryam Jamil, Shannon J Hostetter, Nicholas D Jeffery, Jodi D Smith, Suzanne T Millman, Rebecca L Parsons, Mark T Butt, Sundeep Chandra, Martin T Egeland, Ana B Assis, Hemanth R Nelvagal, Jonathan D Cooper, Igor Nestrasil, Bryon A Mueller, Rene Labounek, Amy Paulson, Heather Prill, Xiao Ying Liu, Huiyu Zhou, Roger Lawrence, Brett E Crawford, Anita Grover, Ganesh Cherala, Andrew C Melton, Anu Cherukuri, Brian R Vuillemenot, Jill CM Wait, Charles A. O'Neill, Jason Pinkstaff, Joseph Kovalchin, Eric Zanelli and Emma McCullagh
Journal of Pharmacology and Experimental Therapeutics June 18, 2022, JPET-AR-2022-001119; DOI: https://doi.org/10.1124/jpet.122.001119
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