Research ArticleDrug Discovery and Translational Medicine
Pharmacology of a central nervous system delivered 2'-O-methoxyethyl-modified survival of motor neuron splicing oligonucleotide in mice and non-human primates
Frank Rigo, Seung J Chun, Daniel A Norris, Gene Hung, Sam Lee, John Matson, Robert A Fey, Hans Gaus, Yimin Hua, John S Grundy, Adrian R Krainer, Scott P Henry and C. Frank Bennett
Journal of Pharmacology and Experimental Therapeutics April 30, 2014, jpet.113.212407; DOI: https://doi.org/10.1124/jpet.113.212407