Research ArticleDrug Discovery and Translational Medicine
Pharmacology of a central nervous system delivered 2'-O-methoxyethyl-modified survival of motor neuron splicing oligonucleotide in mice and non-human primates
Frank Rigo, Seung J Chun, Daniel A Norris, Gene Hung, Sam Lee, John Matson, Robert A Fey, Hans Gaus, Yimin Hua, John S Grundy, Adrian R Krainer, Scott P Henry and C. Frank Bennett
Journal of Pharmacology and Experimental Therapeutics April 30, 2014, jpet.113.212407; DOI: https://doi.org/10.1124/jpet.113.212407
Frank Rigo
1 ISIS Pharmaceuticals;
Seung J Chun
1 ISIS Pharmaceuticals;
Daniel A Norris
1 ISIS Pharmaceuticals;
Gene Hung
1 ISIS Pharmaceuticals;
Sam Lee
1 ISIS Pharmaceuticals;
John Matson
1 ISIS Pharmaceuticals;
Robert A Fey
1 ISIS Pharmaceuticals;
Hans Gaus
1 ISIS Pharmaceuticals;
Yimin Hua
2 Cold Spring Harbor Laboratory
John S Grundy
1 ISIS Pharmaceuticals;
Adrian R Krainer
2 Cold Spring Harbor Laboratory
Scott P Henry
1 ISIS Pharmaceuticals;
C. Frank Bennett
1 ISIS Pharmaceuticals;
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In this issue
Research ArticleDrug Discovery and Translational Medicine
Pharmacology of a central nervous system delivered 2'-O-methoxyethyl-modified survival of motor neuron splicing oligonucleotide in mice and non-human primates
Frank Rigo, Seung J Chun, Daniel A Norris, Gene Hung, Sam Lee, John Matson, Robert A Fey, Hans Gaus, Yimin Hua, John S Grundy, Adrian R Krainer, Scott P Henry and C. Frank Bennett
Journal of Pharmacology and Experimental Therapeutics April 30, 2014, jpet.113.212407; DOI: https://doi.org/10.1124/jpet.113.212407
Research ArticleDrug Discovery and Translational Medicine
Pharmacology of a central nervous system delivered 2'-O-methoxyethyl-modified survival of motor neuron splicing oligonucleotide in mice and non-human primates
Frank Rigo, Seung J Chun, Daniel A Norris, Gene Hung, Sam Lee, John Matson, Robert A Fey, Hans Gaus, Yimin Hua, John S Grundy, Adrian R Krainer, Scott P Henry and C. Frank Bennett
Journal of Pharmacology and Experimental Therapeutics April 30, 2014, jpet.113.212407; DOI: https://doi.org/10.1124/jpet.113.212407
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